Newborn Screening Advocacy Succeeds in Georgia Earlier this month, Georgia Governor Brian Kemp signed HB 567 [ https://www.legis.ga.gov/legislation/59896 ] into law, which will require the state to consider new federal newborn screening (NBS) recommendations within one year, implement them within two and a half years, and provide appropriate funding for the NBS program. ASGCT supported the bill…

Vertex and CRISPR Therapeutics Present New Data in 22 Patients With Greater Than 3 Months Follow-Up Post-Treatment With Investigational CRISPR/Cas9 Gene-Editing Therapy, CTX001™ at European Hematology Association Annual Meeting – Beta thalassemia: All 15 patients were transfusion independent after CTX001 infusion – – Sickle cell disease: All seven patients were free of vaso-occlusive crises after…

Passing on Sickle Cell to your Children Warrior parents, can you relate to feeling like this? How do you cope? What helps you get through these feelings about passing on sickle cell? Jourdan Dunn feels as if she passed sickle cell disease on to her son, Riley Dunn. The model-turned-actress recently told The Sunday Times magazine about…